| 1 |
33145772 | Cardiac pathology in mucopolysaccharidosis I mice: Losartan modifies ERK1/2 activation during cardiac remodeling. | 2021 May |
1 |
| 2 |
33319323 | Morphological damage in Sertoli, myoid and interstitial cells in a mouse model of mucopolysaccharidosis type I (MPS I). | 2021 Jan |
4 |
| 3 |
33434858 | Biomechanical and histological characterization of MPS I mice femurs. | 2021 Feb |
2 |
| 4 |
31679559 | Evidence that glycosaminoglycan storage and collagen deposition in the cauda epididymidis does not impair sperm viability in the Mucopolysaccharidosis type I mouse model. | 2020 Feb |
3 |
| 5 |
32162173 | Morphologic description of male reproductive accessory glands in a mouse model of mucopolysaccharidosis type I (MPS I). | 2020 Apr |
1 |
| 6 |
32439268 | Neonatal combination therapy improves some of the clinical manifestations in the Mucopolysaccharidosis type I murine model. | 2020 Jul |
1 |
| 7 |
30528089 | ZFN-Mediated In Vivo Genome Editing Corrects Murine Hurler Syndrome. | 2019 Jan 2 |
3 |
| 8 |
31065277 | Induced Pluripotent Stem Cell Derivation and Ex Vivo Gene Correction Using a Mucopolysaccharidosis Type 1 Disease Mouse Model. | 2019 |
2 |
| 9 |
31834922 | Sexual behaviour in a murine model of mucopolysaccharidosis type I (MPS I). | 2019 |
2 |
| 10 |
28882767 | Optimization of alginate microcapsules containing cells overexpressing α-l-iduronidase using Box-Behnken design. | 2018 Jan 1 |
4 |
| 11 |
29198892 | RTB lectin-mediated delivery of lysosomal α-l-iduronidase mitigates disease manifestations systemically including the central nervous system. | 2018 Feb |
1 |
| 12 |
29940298 | Intra-articular nonviral gene therapy in mucopolysaccharidosis I mice. | 2018 Sep 5 |
2 |
| 13 |
28150116 | Subcutaneous implantation of microencapsulated cells overexpressing α-L-iduronidase for mucopolysaccharidosis type I treatment. | 2017 Mar |
4 |
| 14 |
28585336 | Liver-Directed Human Amniotic Epithelial Cell Transplantation Improves Systemic Disease Phenotype in Hurler Syndrome Mouse Model. | 2017 Jul |
2 |
| 15 |
28958576 | Guanidinylated Neomycin Conjugation Enhances Intranasal Enzyme Replacement in the Brain. | 2017 Dec 6 |
2 |
| 16 |
27720939 | Differential expression of microRNAs from miR-17 family in the cerebellum of mucopolysaccharidosis type I mice. | 2016 Dec 31 |
1 |
| 17 |
25541102 | Shotgun proteomics reveals possible mechanisms for cognitive impairment in Mucopolysaccharidosis I mice. | 2015 Feb |
4 |
| 18 |
26407983 | Decreased performance in IDUA knockout mouse mimic limitations of joint function and locomotion in patients with Hurler syndrome. | 2015 Sep 25 |
1 |
| 19 |
28649535 | Characterization of the MPS I-H knock-in mouse reveals increased femoral biomechanical integrity with compromised material strength and altered bone geometry. | 2015 Dec |
1 |
| 20 |
22983812 | Retroviral-vector-mediated gene therapy to mucopolysaccharidosis I mice improves sensorimotor impairments and other behavioral deficits. | 2013 May |
4 |
| 21 |
23593225 | Attenuation of nonsense-mediated mRNA decay enhances in vivo nonsense suppression. | 2013 |
2 |
| 22 |
22056610 | The designer aminoglycoside NB84 significantly reduces glycosaminoglycan accumulation associated with MPS I-H in the Idua-W392X mouse. | 2012 Jan |
3 |
| 23 |
22520214 | Treatment of adult MPSI mouse brains with IDUA-expressing mesenchymal stem cells decreases GAG deposition and improves exploratory behavior. | 2012 Apr 20 |
5 |
| 24 |
21081900 | Minicircle DNA-based gene therapy coupled with immune modulation permits long-term expression of α-L-iduronidase in mice with mucopolysaccharidosis type I. | 2011 Mar |
1 |
| 25 |
21253856 | Lipid composition of whole brain and cerebellum in Hurler syndrome (MPS IH) mice. | 2011 Sep |
1 |
| 26 |
21965007 | Genomic instability in blood cells from murine model of mucopolysaccharidosis type I. | 2011 Dec |
1 |
| 27 |
20847202 | Gene therapy augments the efficacy of hematopoietic cell transplantation and fully corrects mucopolysaccharidosis type I phenotype in the mouse model. | 2010 Dec 9 |
1 |
| 28 |
19384290 | Systemic correction of storage disease in MPS I NOD/SCID mice using the sleeping beauty transposon system. | 2009 Jul |
2 |
| 29 |
18613275 | Improved retroviral vector design results in sustained expression after adult gene therapy in mucopolysaccharidosis I mice. | 2008 Sep |
4 |
| 30 |
16979922 | Effect of neonatal administration of a retroviral vector expressing alpha-L-iduronidase upon lysosomal storage in brain and other organs in mucopolysaccharidosis I mice. | 2007 Feb |
2 |
| 31 |
17311010 | Improvements in mucopolysaccharidosis I mice after adult retroviral vector-mediated gene therapy with immunomodulation. | 2007 May |
2 |
| 32 |
17920451 | Characterization of an immunodeficient mouse model of mucopolysaccharidosis type I suitable for preclinical testing of human stem cell and gene therapy. | 2007 Nov 1 |
4 |
| 33 |
17044753 | Limited transgene immune response and long-term expression of human alpha-L-iduronidase in young adult mice with mucopolysaccharidosis type I by liver-directed gene therapy. | 2006 Nov |
2 |
| 34 |
15585404 | Liver-directed neonatal gene therapy prevents cardiac, bone, ear, and eye disease in mucopolysaccharidosis I mice. | 2005 Jan |
2 |
| 35 |
15703491 | Gene therapy for a mucopolysaccharidosis type I murine model with lentiviral-IDUA vector. | 2005 Jan |
1 |
| 36 |
15851016 | Neonatal gene therapy of MPS I mice by intravenous injection of a lentiviral vector. | 2005 May |
1 |
| 37 |
16435197 | Nonviral in vivo gene transfer in the mucopolysaccharidosis I murine model. | 2005 |
1 |
| 38 |
12948739 | Treatment of the mouse model of mucopolysaccharidosis I with retrovirally transduced bone marrow. | 2003 Aug |
1 |
| 39 |
9097952 | Murine mucopolysaccharidosis type I: targeted disruption of the murine alpha-L-iduronidase gene. | 1997 Apr |
1 |