Title : Subcutaneous implantation of microencapsulated cells overexpressing α-L-iduronidase for mucopolysaccharidosis type I treatment.

Pub. Date : 2017 Mar

PMID : 28150116






4 Functional Relationships(s)
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Compound Name
Protein Name
Organism
1 Mucopolysaccharidosis type I (MPS I) is caused by a deficiency of alpha-L-iduronidase (IDUA), resulting in accumulation of glycosaminoglycans (GAG) in lysosomes. Glycosaminoglycans iduronidase, alpha-L Mus musculus
2 Mucopolysaccharidosis type I (MPS I) is caused by a deficiency of alpha-L-iduronidase (IDUA), resulting in accumulation of glycosaminoglycans (GAG) in lysosomes. Glycosaminoglycans iduronidase, alpha-L Mus musculus
3 Mucopolysaccharidosis type I (MPS I) is caused by a deficiency of alpha-L-iduronidase (IDUA), resulting in accumulation of glycosaminoglycans (GAG) in lysosomes. Glycosaminoglycans iduronidase, alpha-L Mus musculus
4 Mucopolysaccharidosis type I (MPS I) is caused by a deficiency of alpha-L-iduronidase (IDUA), resulting in accumulation of glycosaminoglycans (GAG) in lysosomes. Glycosaminoglycans iduronidase, alpha-L Mus musculus