4 Article(s)Download |
PMID | Title | Pub. Year | #Total Relationships |
| 1 | 34712574 | Impaired neural differentiation of MPS IIIA patient induced pluripotent stem cell-derived neural progenitor cells. | 2021 Dec | 2 |
| 2 | 27331076 | Functional correction of neurological and somatic disorders at later stages of disease in MPS IIIA mice by systemic scAAV9-hSGSH gene delivery. | 2016 | 2 |
| 3 | 27491210 | Brain Targeting in MPS-IIIA. | 2016 Jun | 1 |
| 4 | 23863627 | Whole body correction of mucopolysaccharidosis IIIA by intracerebrospinal fluid gene therapy. | 2013 Aug 1 | 1 |