| 1 |
33586684 | ActRIIB:ALK4-Fc alleviates muscle dysfunction and comorbidities in murine models of neuromuscular disorders. | 2021 Feb 15 |
1 |
| 2 |
33606217 | Antisense Oligonucleotide Treatment in a Humanized Mouse Model of Duchenne Muscular Dystrophy and Highly Sensitive Detection of Dystrophin Using Western Blotting. | 2021 |
1 |
| 3 |
34151854 | Revertant Phenomenon in DMD and LGMD2I and Its Therapeutic Implications: A Review of Study Under Mentorship of Terrence Partridge. | 2021 |
1 |
| 4 |
34832896 | Intramuscular Evaluation of Chimeric Locked Nucleic Acid/2'OMethyl-Modified Antisense Oligonucleotides for Targeted Exon 23 Skipping in Mdx Mice. | 2021 Oct 30 |
1 |
| 5 |
32244535 | Alpha-l-Locked Nucleic Acid-Modified Antisense Oligonucleotides Induce Efficient Splice Modulation In Vitro. | 2020 Mar 31 |
1 |
| 6 |
32350552 | Noncoding RNAs in Duchenne and Becker muscular dystrophies: role in pathogenesis and future prognostic and therapeutic perspectives. | 2020 Nov |
1 |
| 7 |
33362201 | Detailed genetic and functional analysis of the hDMDdel52/mdx mouse model. | 2020 |
1 |
| 8 |
30281092 | Cmah-dystrophin deficient mdx mice display an accelerated cardiac phenotype that is improved following peptide-PMO exon skipping treatment. | 2019 Feb 1 |
1 |
| 9 |
29067663 | The Use of Antisense Oligonucleotides for the Treatment of Duchenne Muscular Dystrophy. | 2018 |
2 |
| 10 |
29466448 | A dystrophic Duchenne mouse model for testing human antisense oligonucleotides. | 2018 |
1 |
| 11 |
29669851 | Systemic administration of the antisense oligonucleotide NS-065/NCNP-01 for skipping of exon 53 in patients with Duchenne muscular dystrophy. | 2018 Apr 18 |
1 |
| 12 |
29789502 | Detection of Dystrophin Dp71 in Human Skeletal Muscle Using an Automated Capillary Western Assay System. | 2018 May 23 |
2 |
| 13 |
29858053 | Repurposing Dantrolene for Long-Term Combination Therapy to Potentiate Antisense-Mediated DMD Exon Skipping in the mdx Mouse. | 2018 Jun 1 |
1 |
| 14 |
30171546 | Exon 51 Skipping Quantification by Digital Droplet PCR in del52hDMD/mdx Mice. | 2018 |
1 |
| 15 |
30396145 | Shorter Phosphorodiamidate Morpholino Splice-Switching Oligonucleotides May Increase Exon-Skipping Efficacy in DMD. | 2018 Dec 7 |
1 |
| 16 |
29246319 | Link between MHC Fiber Type and Restoration of Dystrophin Expression and Key Components of the DAPC by Tricyclo-DNA-Mediated Exon Skipping. | 2017 Dec 15 |
1 |
| 17 |
25758104 | Prevention of exercised induced cardiomyopathy following Pip-PMO treatment in dystrophic mdx mice. | 2015 Mar 11 |
1 |
| 18 |
25959011 | Combination Antisense Treatment for Destructive Exon Skipping of Myostatin and Open Reading Frame Rescue of Dystrophin in Neonatal mdx Mice. | 2015 Aug |
1 |
| 19 |
26594036 | Identification of novel, therapy-responsive protein biomarkers in a mouse model of Duchenne muscular dystrophy by aptamer-based serum proteomics. | 2015 Nov 23 |
1 |
| 20 |
23634945 | Dose-dependent pharmacokinetic profiles of 2'-O-methyl phosphorothioate antisense oligonucleotidesin mdx mice. | 2013 Jun |
1 |
| 21 |
23658612 | Effective exon skipping and dystrophin restoration by 2'-o-methoxyethyl antisense oligonucleotide in dystrophin-deficient mice. | 2013 |
2 |
| 22 |
24057032 | Generation of embryonic stem cells and mice for duchenne research. | 2013 Sep 10 |
1 |
| 23 |
22533380 | Antisense oligonucleotide-mediated exon skipping for Duchenne muscular dystrophy: progress and challenges. | 2012 Jun |
1 |
| 24 |
21505427 | Pip5 transduction peptides direct high efficiency oligonucleotide-mediated dystrophin exon skipping in heart and phenotypic correction in mdx mice. | 2011 Jul |
2 |
| 25 |
21851223 | Long-term systemic administration of unconjugated morpholino oligomers for therapeutic expression of dystrophin by exon skipping in skeletal muscle: implications for cardiac muscle integrity. | 2011 Aug |
1 |
| 26 |
22277414 | [Exon-skipping therapy for Duchenne muscular dystrophy]. | 2011 Nov |
1 |
| 27 |
20068555 | Optimization of peptide nucleic acid antisense oligonucleotides for local and systemic dystrophin splice correction in the mdx mouse. | 2010 Apr |
1 |
| 28 |
20407428 | Preclinical PK and PD studies on 2'-O-methyl-phosphorothioate RNA antisense oligonucleotides in the mdx mouse model. | 2010 Jun |
1 |
| 29 |
20542988 | Site-directed gene repair of the dystrophin gene mediated by PNA-ssODNs. | 2010 Aug 15 |
1 |
| 30 |
20700113 | Functional rescue of dystrophin-deficient mdx mice by a chimeric peptide-PMO. | 2010 Oct |
1 |
| 31 |
18784750 | Microwave irradiation enhances gene and oligonucleotide delivery and induces effective exon skipping in myoblasts. | 2009 Jan |
1 |
| 32 |
19236710 | Genetic correction of splice site mutation in purified and enriched myoblasts isolated from mdx5cv mice. | 2009 Feb 23 |
1 |
| 33 |
19288467 | Efficacy of systemic morpholino exon-skipping in Duchenne dystrophy dogs. | 2009 Jun |
1 |
| 34 |
19469709 | Dosing regimen has a significant impact on the efficiency of morpholino oligomer-induced exon skipping in mdx mice. | 2009 Sep |
2 |
| 35 |
19692354 | A fusion peptide directs enhanced systemic dystrophin exon skipping and functional restoration in dystrophin-deficient mdx mice. | 2009 Nov 15 |
2 |
| 36 |
20030230 | [Exon skipping therapy for Duchenne muscular dystrophy by using antisense Morpholino]. | 2009 Nov |
2 |
| 37 |
17968354 | Effective exon skipping and restoration of dystrophin expression by peptide nucleic acid antisense oligonucleotides in mdx mice. | 2008 Jan |
2 |
| 38 |
18499783 | Long-term administration of antisense oligonucleotides into the paraspinal muscles of mdx mice reduces kyphosis. | 2008 Aug |
1 |
| 39 |
18647087 | Functionalized PEG-PEI copolymers complexed to exon-skipping oligonucleotides improve dystrophin expression in mdx mice. | 2008 Aug |
1 |
| 40 |
18784278 | Cell-penetrating peptide-conjugated antisense oligonucleotides restore systemic muscle and cardiac dystrophin expression and function. | 2008 Dec 15 |
1 |
| 41 |
17555369 | Potential of oligonucleotide-mediated exon-skipping therapy for Duchenne muscular dystrophy. | 2007 Jun |
1 |
| 42 |
17579573 | Morpholino oligomer-mediated exon skipping averts the onset of dystrophic pathology in the mdx mouse. | 2007 Sep |
1 |
| 43 |
18646569 | Optimizing exon skipping therapies for DMD. | 2007 Dec |
2 |
| 44 |
16285002 | Dystrophin expression in the mdx mouse after localised and systemic administration of a morpholino antisense oligonucleotide. | 2006 Feb |
4 |
| 45 |
16488666 | Induction of dystrophin expression by exon skipping in mdx mice following intramuscular injection of antisense oligonucleotides complexed with PEG-PEI copolymers. | 2006 Jul |
2 |
| 46 |
16719929 | Induction of revertant fibres in the mdx mouse using antisense oligonucleotides. | 2006 May 24 |
1 |
| 47 |
15563511 | Strand bias in oligonucleotide-mediated dystrophin gene editing. | 2005 Jan 15 |
1 |
| 48 |
15608067 | Systemic delivery of antisense oligoribonucleotide restores dystrophin expression in body-wide skeletal muscles. | 2005 Jan 4 |
1 |
| 49 |
15386737 | Towards a therapeutic inhibition of dystrophin exon 23 splicing in mdx mouse muscle induced by antisense oligoribonucleotides (splicomers): target sequence optimisation using oligonucleotide arrays. | 2004 Oct |
1 |
| 50 |
12874101 | Morpholino antisense oligonucleotide induced dystrophin exon 23 skipping in mdx mouse muscle. | 2003 Aug 1 |
1 |