| 1 |
34698059 | Renadirsen, a Novel 2'OMeRNA/ENA® Chimera Antisense Oligonucleotide, Induces Robust Exon 45 Skipping for Dystrophin In Vivo. | 2021 Sep 25 |
1 |
| 2 |
30972156 | Antisense oligonucleotides for the treatment of cardiomyopathy in Duchenne muscular dystrophy. | 2019 |
1 |
| 3 |
29067660 | Exon Skipping Therapy Using Phosphorodiamidate Morpholino Oligomers in the mdx52 Mouse Model of Duchenne Muscular Dystrophy. | 2018 |
1 |
| 4 |
30171552 | Systemic Intravenous Administration of Antisense Therapeutics for Combinatorial Dystrophin and Myostatin Exon Splice Modulation. | 2018 |
1 |
| 5 |
28208626 | 2'-O-Methyl RNA/Ethylene-Bridged Nucleic Acid Chimera Antisense Oligonucleotides to Induce Dystrophin Exon 45 Skipping. | 2017 Feb 10 |
2 |
| 6 |
27398133 | Recent advances in innovative therapeutic approaches for Duchenne muscular dystrophy: from discovery to clinical trials. | 2016 |
1 |
| 7 |
25791417 | Phosphorothioate modification of chimeric 2´-O-methyl RNA/ethylene-bridged nucleic acid oligonucleotides increases dystrophin exon 45 skipping capability and reduces cytotoxicity. | 2015 Feb 17 |
2 |
| 8 |
24380394 | Skipping multiple exons of dystrophin transcripts using cocktail antisense oligonucleotides. | 2014 Feb |
1 |
| 9 |
22274137 | Novel cationic carotenoid lipids as delivery vectors of antisense oligonucleotides for exon skipping in Duchenne muscular dystrophy. | 2012 Jan 24 |
1 |
| 10 |
22454059 | Optimizing RNA/ENA chimeric antisense oligonucleotides using in vitro splicing. | 2012 |
1 |
| 11 |
22454060 | Optimizing antisense oligonucleotides using phosphorodiamidate morpholino oligomers. | 2012 |
1 |
| 12 |
22486275 | A prospective study in the rational design of efficient antisense oligonucleotides for exon skipping in the DMD gene. | 2012 Jul |
1 |
| 13 |
21967521 | Antisense oligonucleotide induced dystrophin exon 45 skipping at a low half-maximal effective concentration in a cell-free splicing system. | 2011 Oct |
1 |
| 14 |
20068555 | Optimization of peptide nucleic acid antisense oligonucleotides for local and systemic dystrophin splice correction in the mdx mouse. | 2010 Apr |
1 |
| 15 |
20079639 | Comparative analysis of antisense oligonucleotide sequences targeting exon 53 of the human DMD gene: Implications for future clinical trials. | 2010 Feb |
3 |
| 16 |
20424011 | Toward an oligonucleotide therapy for Duchenne muscular dystrophy: a complex development challenge. | 2010 Mar 31 |
1 |
| 17 |
19142179 | Design of phosphorodiamidate morpholino oligomers (PMOs) for the induction of exon skipping of the human DMD gene. | 2009 Mar |
1 |
| 18 |
19351396 | Formulation of polylactide-co-glycolic acid nanospheres for encapsulation and sustained release of poly(ethylene imine)-poly(ethylene glycol) copolymers complexed to oligonucleotides. | 2009 Apr 7 |
1 |
| 19 |
19760747 | Exon skipping-mediated dystrophin reading frame restoration for small mutations. | 2009 Nov |
1 |
| 20 |
18784278 | Cell-penetrating peptide-conjugated antisense oligonucleotides restore systemic muscle and cardiac dystrophin expression and function. | 2008 Dec 15 |
1 |
| 21 |
17285139 | Antisense oligonucleotide-induced exon skipping across the human dystrophin gene transcript. | 2007 Jul |
2 |
| 22 |
17601349 | Antisense oligonucleotide induced exon skipping and the dystrophin gene transcript: cocktails and chemistries. | 2007 Jul 2 |
2 |
| 23 |
17767400 | Comparative analysis of antisense oligonucleotide sequences for targeted skipping of exon 51 during dystrophin pre-mRNA splicing in human muscle. | 2007 Sep |
1 |
| 24 |
16919955 | Induced dystrophin exon skipping in human muscle explants. | 2006 Oct |
1 |
| 25 |
15536518 | Antisense oligonucleotides and short interfering RNAs silencing the cyclin-dependent kinase inhibitor p21 improve proliferation of Duchenne muscular dystrophy patients' primary skeletal myoblasts. | 2005 Jan |
1 |
| 26 |
16259564 | Poly(ethylene imine)-poly(ethylene glycol) copolymers facilitate efficient delivery of antisense oligonucleotides to nuclei of mature muscle cells of mdx mice. | 2005 Nov |
1 |
| 27 |
14527677 | Enhanced in vivo delivery of antisense oligonucleotides to restore dystrophin expression in adult mdx mouse muscle. | 2003 Sep 25 |
1 |