N-acetylgalactosaminuronic acid

5'-aminolevulinate synthase 1 ; Homo sapiens







3 Article(s)
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1 33941543 Nonclinical Pharmacokinetics and Absorption, Distribution, Metabolism, and Excretion of Givosiran, the First Approved N-Acetylgalactosamine-Conjugated RNA Interference Therapeutic. 2021 Jul 2
2 31792921 Leading RNA Interference Therapeutics Part 2: Silencing Delta-Aminolevulinic Acid Synthase 1, with a Focus on Givosiran. 2020 Feb 1
3 26528940 Preclinical Development of a Subcutaneous ALAS1 RNAi Therapeutic for Treatment of Hepatic Porphyrias Using Circulating RNA Quantification. 2015 Nov 3 1