| 1 |
35121108 | Fluoxetine ameliorates mucopolysaccharidosis type IIIA. | 2022 Apr 6 |
1 |
| 2 |
30907009 | Early disease course is unaltered in mucopolysaccharidosis type IIIA (MPS IIIA) mice lacking α-synuclein. | 2019 Dec |
1 |
| 3 |
31020862 | An Improved Adeno-Associated Virus Vector for Neurological Correction of the Mouse Model of Mucopolysaccharidosis IIIA. | 2019 Sep |
1 |
| 4 |
27585464 | Glycosaminoglycan levels and structure in a mucopolysaccharidosis IIIA mice and the effect of a highly secreted sulfamidase engineered to cross the blood-brain barrier. | 2017 Feb |
4 |
| 5 |
28601604 | Axonal dystrophy in the brain of mice with Sanfilippo syndrome. | 2017 Sep |
1 |
| 6 |
26626972 | Low-dose, continual enzyme delivery ameliorates some aspects of established brain disease in a mouse model of a childhood-onset neurodegenerative disorder. | 2016 Apr |
1 |
| 7 |
26975339 | A Preclinical Study Evaluating AAVrh10-Based Gene Therapy for Sanfilippo Syndrome. | 2016 May |
1 |
| 8 |
23748415 | Myeloid/Microglial driven autologous hematopoietic stem cell gene therapy corrects a neuronopathic lysosomal disease. | 2013 Oct |
4 |
| 9 |
23022219 | Exocytosis is impaired in mucopolysaccharidosis IIIA mouse chromaffin cells. | 2012 Dec 27 |
1 |
| 10 |
19302155 | Examination of intravenous and intra-CSF protein delivery for treatment of neurological disease. | 2009 Mar |
1 |
| 11 |
18518922 | Effect of high dose, repeated intra-cerebrospinal fluid injection of sulphamidase on neuropathology in mucopolysaccharidosis type IIIA mice. | 2008 Oct |
4 |
| 12 |
17227588 | Lentiviral-mediated gene correction of mucopolysaccharidosis type IIIA. | 2007 Jan 16 |
1 |
| 13 |
17725987 | Functional correction of CNS lesions in an MPS-IIIA mouse model by intracerebral AAV-mediated delivery of sulfamidase and SUMF1 genes. | 2007 Nov 15 |
2 |
| 14 |
12801641 | Mouse sulphamidase gene: characterization of the promoter region of the gene and expression in mouse tissues. | 2003 May 22 |
1 |
| 15 |
10818207 | Gene encoding the mouse sulphamidase: cDNA cloning, structure, and chromosomal mapping. | 2000 Jun |
1 |