Pub. Date : 2019 Jun 13
PMID : 31196016
4 Functional Relationships(s)Download |
Sentence | Compound Name | Protein Name | Organism |
1 | Evaluation of long-term effectiveness of the use of carglumic acid in patients with propionic acidemia (PA) or methylmalonic acidemia (MMA): study protocol for a randomized controlled trial. | carglumic acid | monocyte to macrophage differentiation associated | Homo sapiens |
2 | Here we report the rationale and design of a phase IIIb trial that is aimed at determining the long-term efficacy and safety of carglumic acid in the management of PA and MMA. | carglumic acid | monocyte to macrophage differentiation associated | Homo sapiens |
3 | Although retrospective studies have suggested that long-term carglumic acid may be beneficial in the management of PA and MMA, current literature lacks evidence for this indication. | carglumic acid | monocyte to macrophage differentiation associated | Homo sapiens |
4 | This clinical trial will determine the long-term safety and efficacy of carglumic acid in the management of PA and MMA. | carglumic acid | monocyte to macrophage differentiation associated | Homo sapiens |