Pub. Date : 2019 Apr 18
PMID : 30995372
2 Functional Relationships(s)Download |
Sentence | Compound Name | Protein Name | Organism |
| 1 | Lentiviral Gene Therapy Combined with Low-Dose Busulfan in Infants with SCID-X1. | Busulfan | interleukin 2 receptor subunit gamma | Homo sapiens |
| 2 | CONCLUSIONS: Lentiviral vector gene therapy combined with low-exposure, targeted busulfan conditioning in infants with newly diagnosed SCID-X1 had low-grade acute toxic effects and resulted in multilineage engraftment of transduced cells, reconstitution of functional T cells and B cells, and normalization of NK-cell counts during a median follow-up of 16 months. | Busulfan | interleukin 2 receptor subunit gamma | Homo sapiens |