Pub. Date : 2018 Apr
PMID : 29620999
2 Functional Relationships(s)Download |
Sentence | Compound Name | Protein Name | Organism |
1 | Dose-Dependent Lowering of Mutant Huntingtin Using Antisense Oligonucleotides in Huntington Disease Patients. | Oligonucleotides | huntingtin | Homo sapiens |
2 | The results from this Ionis trial have gained much attention from the patient community and the oligonucleotide therapeutics field, since it is the first trial targeting the cause of HD, namely the mutant huntingtin protein, using antisense oligonucleotides (ASOs). | Oligonucleotides | huntingtin | Homo sapiens |