Title : Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after systemic phosphorodiamidate morpholino oligomer treatment: an open-label, phase 2, dose-escalation study.

Pub. Date : 2011 Aug 13

PMID : 21784508






1 Functional Relationships(s)
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1 Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after systemic phosphorodiamidate morpholino oligomer treatment: an open-label, phase 2, dose-escalation study. DIAMIDOPHOSPHATE dystrophin Homo sapiens