Title : Targeted skipping of human dystrophin exons in transgenic mouse model systemically for antisense drug development.

Pub. Date : 2011

PMID : 21611204






1 Functional Relationships(s)
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1 We also established a GFP-reporter myoblast culture to screen AOs targeting human dystrophin exon 50. D-(+)-ALLOSE dystrophin Homo sapiens