PMID-sentid Pub_year Sent_text comp_official_name comp_offsetprotein_name organism prot_offset 34938609-3 2022 We established a screening platform with human neurons of patients and controls derived from induced pluripotent stem cells to test antisense oligonucleotides (ASOs) for their effects on ataxin-3 expression. Oligonucleotides, Antisense 160-164 ataxin 3 Homo sapiens 187-195 28624196-3 2017 Here we tested antisense oligonucleotides (ASOs) that target human ATXN3 in two complementary mouse models of SCA3: yeast artificial chromosome (YAC) MJD-Q84.2 (Q84) mice expressing the full-length human ATXN3 gene and cytomegalovirus (CMV) MJD-Q135 (Q135) mice expressing a human ATXN3 cDNA. Oligonucleotides, Antisense 43-47 ataxin 3 Homo sapiens 67-72