1 Article(s)Download |
PMID | Title | Pub. Year | #Total Relationships |
| 1 | 28803710 | Intrathecal 2-hydroxypropyl-β-cyclodextrin decreases neurological disease progression in Niemann-Pick disease, type C1: a non-randomised, open-label, phase 1-2 trial. | 2017 Oct 14 | 1 |