| 1 |
33230432 | Morpholino Oligomer-Induced Dystrophin Isoforms to Map the Functional Domains in the Dystrophin Protein. | 2020 Dec 4 |
1 |
| 2 |
33285037 | Viltolarsen in Japanese Duchenne muscular dystrophy patients: A phase 1/2 study. | 2020 Dec |
1 |
| 3 |
31322741 | Autoimmune response and its long-term consequences after exon-skipping therapy in a Duchenne muscular dystrophy mouse model. | 2019 Nov |
1 |
| 4 |
31416775 | Exons 45-55 Skipping Using Mutation-Tailored Cocktails of Antisense Morpholinos in the DMD Gene. | 2019 Nov 6 |
1 |
| 5 |
24942628 | Exon skipping restores dystrophin expression, but fails to prevent disease progression in later stage dystrophic dko mice. | 2014 Sep |
1 |
| 6 |
22683468 | Long-term rescue of dystrophin expression and improvement in muscle pathology and function in dystrophic mdx mice by peptide-conjugated morpholino. | 2012 Aug |
1 |