PMID-sentid Pub_year Sent_text comp_official_name comp_offsetprotein_name organism prot_offset 31594243-21 2019 CONCLUSIONS: This prospective observational study indicates a mild treatment effect in adults with long-standing SMA3 after 10 months of treatment with Nusinersen, which had never occurred in the natural history of the disease. nusinersen 152-162 GUSB pseudogene 14 Homo sapiens 113-117