Title : Lipid nanoparticle delivers phenylalanine ammonia lyase mRNA to the liver leading to catabolism and clearance of phenylalanine in a phenylketonuria mouse model.

Pub. Date : 2022 Sep

PMID : 35600090






1 Functional Relationships(s)
Download
Sentence
Compound Name
Protein Name
Organism
1 Without a functional copy of PAH, levels of Phe in the blood and tissues rise, resulting in potentially life-threatening damage to the central nervous system. Phenylalanine phenylalanine hydroxylase Homo sapiens