Title : Systems Approaches to Unravel Molecular Function: High-content siRNA Screen Identifies TMEM16A Traffic Regulators as Potential Drug Targets for Cystic Fibrosis.

Pub. Date : 2022 Mar 15

PMID : 34990652






1 Functional Relationships(s)
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1 An attractive approach to treat people with Cystic Fibrosis (CF), a life-shortening disease caused by mutant CFTR, is to compensate for the absence of this chloride/bicarbonate channel by activating alternative (non-CFTR) chloride channels. Bicarbonates CF transmembrane conductance regulator Homo sapiens