Title : Extracellular vesicles from recombinant cell factories improve the activity and efficacy of enzymes defective in lysosomal storage disorders.

Pub. Date : 2021 Mar

PMID : 33738082






1 Functional Relationships(s)
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1 Moreover, a single intravenous administration of EV-GLA was able to reduce globotriaosylceramide (Gb3) substrate levels in clinically relevant tissues, such kidneys and brain. globotriaosylceramide alpha 1,4-galactosyltransferase (P blood group) Homo sapiens