Title : A G542X cystic fibrosis mouse model for examining nonsense mutation directed therapies.

Pub. Date : 2018

PMID : 29924856






1 Functional Relationships(s)
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1 Importantly, CFTR restoration is observed in G542X intestinal organoids treated with G418, an aminoglycoside with translational readthrough capabilities. antibiotic G 418 cystic fibrosis transmembrane conductance regulator Mus musculus