Title : rAAV-CFTRΔR Rescues the Cystic Fibrosis Phenotype in Human Intestinal Organoids and Cystic Fibrosis Mice.

Pub. Date : 2016 Feb 1

PMID : 26509335






2 Functional Relationships(s)
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1 A rescue in chloride and fluid secretion after rAAV-CFTRDeltaR treatment was assessed by forskolin-induced swelling in CF transmembrane conductance regulator (CFTR)-deficient organoids and by nasal potential differences in DeltaF508 mice. Colforsin cystic fibrosis transmembrane conductance regulator Mus musculus
2 A rescue in chloride and fluid secretion after rAAV-CFTRDeltaR treatment was assessed by forskolin-induced swelling in CF transmembrane conductance regulator (CFTR)-deficient organoids and by nasal potential differences in DeltaF508 mice. Colforsin cystic fibrosis transmembrane conductance regulator Mus musculus