Title : Promoter-specific lentivectors for long-term, cardiac-directed therapy of Fabry disease.

Pub. Date : 2011 Jan

PMID : 20846825






4 Functional Relationships(s)
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Compound Name
Protein Name
Organism
1 In Fabry disease a deficiency of alpha-galactosidase A (alpha-gal A) activity leads to accumulation of globotriaosylceramide (Gb3) in various tissues including the heart. globotriaosylceramide galactosidase, alpha Mus musculus
2 In Fabry disease a deficiency of alpha-galactosidase A (alpha-gal A) activity leads to accumulation of globotriaosylceramide (Gb3) in various tissues including the heart. globotriaosylceramide galactosidase, alpha Mus musculus
3 In Fabry disease a deficiency of alpha-galactosidase A (alpha-gal A) activity leads to accumulation of globotriaosylceramide (Gb3) in various tissues including the heart. globotriaosylceramide galactosidase, alpha Mus musculus
4 In Fabry disease a deficiency of alpha-galactosidase A (alpha-gal A) activity leads to accumulation of globotriaosylceramide (Gb3) in various tissues including the heart. globotriaosylceramide galactosidase, alpha Mus musculus